Patients’ involvement in clinical trial design
We have already highlighted in previous steps of this MOOC how patient involvement can boost translational research at different levels. In the following video, we can listen to the testimony …
Course: From Lab to Clinic: Translational Research for Rare Diseases
Why do we need animal models?
In this video, you will learn why animals are useful and currently still irreplaceable for studying pathology and developing therapies.
Rare disease landscape: a few initiatives to help you understand the RD environment
Rare diseases (RD) are conditions that have been historically neglected, because of both their complexity and the rarity of their clinical presentations. There are barriers to establishing a timely diagnosis …
Role of Patient Advocacy Organizations in drug repurposing and a successful repurposing case
The role of people living with a rare disease is fundamental in promoting preclinical and clinical research for rare diseases and this is also true for drug repurposing. Rick Thompson …
What is the role of patients in preclinical research
What’s the role of patients in preclinical research? Patients are not only research subjects and can play a pro-active role in translating research results into health improvements. Let’s hear about …
When to use which model?
This video will go into the aspects that need to be considered to ask the right question to the right model.
These articles are from the online course:
From Lab to Clinic: Translational Research for Rare Diseases